New gene therapy treatment routes for motor neurone disease uncovered in new study -- MEDICA Trade Fair

New gene therapy treatment routes for motor neurone disease uncovered in new study

07/18/2017

image: human genes; copyright: panthermedia.net/krishna creations

The team identified a particular protein called SRSF1 which binds to the pathological repeated RNA molecules and transports them out of the cell centre, effectively overriding the gatekeeping machinery within the nucleus by opening a back door; © panthermedia.net/krishna creations