Groundbreaking gene therapy trial set to cure haemophilia -- MEDICA - World Forum for Medicine

Groundbreaking gene therapy trial set to cure haemophilia

19/12/2017

Image: the word "haemophilia" on white ground; Copyright: panthermedia.net/chrisdorney

There are around 2000 people with severe haemophilia A in the UK. A hereditary genetic condition dominantly affecting men, people with severe haemophilia A have virtually none of the protein factor VIII which is essential for blood to clot.